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susu200213

susu200213

V2EX member #559468, joined on 2021-10-24 01:11:14 +08:00
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@osilinka 找了的,无解
据家族患病历史来看,有尊严的生命周期也就 10 年左右,其实如果让我立马死掉也无所谓了,这种慢慢折磨你,却无能为力的感觉太难受了
安吉白茶
@Akitora 复议
Mar 21
Replied to a topic by MuyuQ 问与答 快被 WSL 整麻了
装 Linux
新进展:这项首个人体临床试验的目标是评估一种名为 VO659 的新研究药物四剂剂量在患有脊髓小脑共济失调 1 型、3 型或亨廷顿舞蹈病的遗传疾病患者的安全性和耐受性。另一个目标是确定该研究药物在单次或多次给药后脑脊髓液和血液中的浓度。研究药物将通过腰椎鞘内注射给药。
打算着手准备申请美国的临床试验申请了
@irisdev 确诊了 SCA3 形 CAG 重复次数 74 次
搜了一周的顶级医学期刊,越搜越不对劲,有懂神经内科的大手子说一下吗
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